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What Is NPC?
About
Research
Resources
Clinical Trials
Active, Not Recruiting
Available
Completed
Recruiting
Unknown Status
Contact
Donate
Phase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease (RAINBOW)
