Archives: Clinical Trials

Study of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease

Open-Label Study of Long-Term Safety and Efficacy of Intravenous Trappsol Cyclo (HPβCD) in Niemann-Pick Disease Type C

Early Access Program With Arimoclomol in US Patients With NPC

Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1

Health Insurance Literacy and Challenges in Accessing Health Services in Niemann-Pick

Induced Pluripotent Stem Cells for Niemann Pick Disease (IPSNPABC)

Hydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease

Miglustat in Niemann-Pick Type C Disease

Study of the Pharmacokinetics of Trappsol and Effects on Potential Biomarkers of Niemann-Pick C1 (NPC1)

Safety and Efficacy of Intravenous Trappsol Cyclo (HPBCD) in Niemann-Pick Type C Patients