Archives: Clinical Trials

Saccadic Eye Movements in Patients With Niemann-Pick Type C Disease

Safety and Efficacy of Miglustat in Chinese NPC Patients

VTS-270 to Treat Niemann-Pick Type C1 (NPC1) Disease

Application of Miglustat in Patients With Niemann-Pick Type C

Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine

N-Acetyl-L-Leucine for Niemann-Pick Disease, Type C (NPC)

A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C

Longitudinal Study of Cognition With Niemann-Pick Disease, Type C (NPC)

Phase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease (RAINBOW)

Arimoclomol Prospective Study in Participants Diagnosed With Niemann-Pick Disease Type C